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Clinical trial condition

Gaucher Disease

Explore clinical trials studying Gaucher Disease. Study availability and eligibility vary by location and protocol.

131 public trials 25 recruiting studies
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Gaucher Disease trial results

Completed

Human Placental-Derived Stem Cell Transplantation

NCT01586455

Conditions
Acute Lymphocytic Leukemia, Acute Myelogenous Leukemia, Adrenal Gland Diseases, +84 more
Locations
  • Children's Hospital Colorado Denver, Colorado, United States
  • New York Medical College Valhalla, New York, United States
  • University of Utah Salt Lake City, Utah, United States
View Trial Details
Completed

Study of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher Disease

NCT02574286

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Cedars Sinai Medical Center Beverly Hills, California, United States
  • Kaiser Permanente Los Angeles, California, United States
  • Emory Genetics Atlanta, Georgia, United States
  • Ann and Robert H Lurie Childrens Hospital of Chicago Chicago, Illinois, United States
View all 15 locations
View Trial Details
Completed

Natural History Study for Pediatric Patients With Early Onset of Either GM1 Gangliosidosis, GM2 Gangliosidoses, or Gaucher Disease Type 2

NCT04470713

Conditions
AB Variant Gangliosidosis GM2, Brain Diseases, Brain Diseases, Metabolic, +24 more
Locations
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Mayo Clinic - Rochester Rochester, Minnesota, United States
  • Lysosomal and Rare Disorders Research and Treatment Center Fairfax, Virginia, United States
  • UCL Cliniques Universitaires Saint-Luc Brussels, Belgium
View all 17 locations
View Trial Details
Completed

A Study of Gene-Activated® Human Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy in Gaucher Disease

NCT00430625

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Hipolito Yrigoyen Buenos Aires, Argentina
  • Shaare Zedek Medical Center Jerusalem, Israel
  • Sociedad Espanola de Socorros Mutuos Asunción, Paraguay
  • National Research Center for Haematology Moscow, Russia
View Trial Details

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