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Gaucher Disease

Clinical trial condition

Gaucher Disease

Explore clinical trials studying Gaucher Disease. Study availability and eligibility vary by location and protocol.

133 public trials 23 recruiting studies

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Gaucher Disease trial results

Recruiting

Study of CAR T-Cells Targeting the GD2 With IL-15+iCaspase9 for Relapsed/Refractory Neuroblastoma or Relapsed/Refractory Osteosarcoma

NCT03721068

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +29 more
Locations: Emory - Winship Cancer Institute Atlanta, Georgia, United States

Lineberger Comprehensive Cancer Center at University of North Carolina - Chapel Hill Chapel Hill, North Carolina, United States

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Recruiting

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

NCT04532047

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +39 more
Locations: University of California San Francisco, California, United States

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Recruiting

GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple Myeloma

NCT05992532

Conditions: Acid Sphingomyelinase Deficiency, Blood Protein Disorders, Brain Diseases, +38 more
Locations: Hospital Universitario de Álava Vitoria-Gasteiz, Alava, Spain

Hospital Universitario Torrecárdenas Almería, Spain

Hospital Son Espases Palma de Mallorca, Balearic Islands, Spain

Hospital Parc Taulí Sabadell, Barcelona, Spain

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Recruiting

Longitudinal Study of Neurodegenerative Disorders

NCT03333200

Conditions: ALD, Alpha-Mannosidosis, Batten Disease, +78 more
Locations: UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States

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Recruiting

A Clinical Study Evaluating LY-M001 Injection in the Treatment of Adult Patients With Type I Gaucher Disease

NCT06818838

Conditions: Anemia, Brain Diseases, Brain Diseases, Metabolic, +18 more
Locations: Guangzhou First People's Hospital Guangzhou, Guangdong, China

Shanxi Bethune Hospital Taiyuan, Shanxi, China

Hematology Hospital, Chinese Academy of Medical Sciences Tianjin, Tianjin Municipality, China

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Recruiting

Institutional Registry of Rare Diseases

NCT06573723

Conditions: Abnormalities, Multiple, Adrenal Gland Diseases, Adrenal Hyperplasia, Congenital, +144 more
Locations: Hospital Italiano de Buenos Aires Buenos Aires, Argentina

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Recruiting

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

NCT04528355

Conditions: Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +119 more
Locations: UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States

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Recruiting

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

NCT01962415

Conditions: Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +125 more
Locations: UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States

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Recruiting

Drug Discovery for Parkinson's With Mutations in the GBA Gene

NCT05536388

Conditions: Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +22 more
Locations: The New York Stem Cell Foundation Research Institute New York, United States

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Recruiting

A Study of the Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients With Gaucher Disease Type I

NCT06162338

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations: The First Affiliated Hospital of Zhejiang University School of Medicine Hanzhou, Zhejiang, China

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