NCT05536388
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +22 more
- Locations
-
- The New York Stem Cell Foundation Research Institute New York, United States
Clinical trial condition
Gaucher Disease
Explore clinical trials studying Gaucher Disease. Study availability and eligibility vary by location and protocol.
131 public trials
25 recruiting studies
Gaucher Disease trial results
NCT06162338
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- The First Affiliated Hospital of Zhejiang University School of Medicine Hanzhou, Zhejiang, China
NCT06539169
- Conditions
- Alpha-Thalassemia, Alzheimer Disease, Amyloidosis, +104 more
- Locations
-
- xCures Los Altos, California, United States
NCT03240653
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- Birmingham Childrens Hospital Birmingham, United Kingdom
- New Queen Elizabeth Hospital Birmingham, United Kingdom
- Cambridge University Hospital Cambridge, United Kingdom
- Great Ormond Street Hospital London, United Kingdom
NCT06272149
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- Xinhua Hospital Affiliated to Shanghai Jiao Tong University School of Medicine Shanghai, Shanghai Municipality, China
Enrolling by Invitation
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
NCT05368038
- Conditions
- Acid Sphingomyelinase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +65 more
- Locations
-
- Maimonides Medical Center Brooklyn, New York, United States
- NYU Langone Hospital - Brooklyn Brooklyn, New York, United States
- North Shore University Hospital Manhasset, New York, United States
- NYU Langone Health - Tisch Hospital New York, United States
Enrolling by Invitation
Genetic Studies of Lysosomal Storage Disorders
NCT00001215
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +21 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Enrolling by Invitation
Effect of Enzyme Replacement Therapy on Cardiac Function in Children With Gaucher Disease Type 3
NCT06627543
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- Ahmed Mohammed Mohammed Asyut, Egypt
Not Yet Recruiting
Study to Evaluate the Efficacy and Safety of Nizubaglustat (AZ-3102) in Patients With Gaucher Disease Type 3 (GD3)
NCT07715084
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- SMS Medical College Jaipur Jaipur, India
- Maula a Azad medical college Delhi New Delhi, India
- Sir Ganga Ram Hospital New Delhi, India
- University of Child Health Sciences and the Children's Hospital Lahore, Pakistan
Not Yet Recruiting
A Phase I/II Clinical Study to Evaluate the Safety and Efficacy of VGN-R08b in Patients With Type III Gaucher's Disease
NCT07603050
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
Not specified
Related conditions
- Brain Diseases (131)
- Brain Diseases, Metabolic (131)
- Brain Diseases, Metabolic, Inborn (131)
- Central Nervous System Diseases (131)
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities (131)
- Lysosomal Storage Diseases, Nervous System (131)
- Nervous System Diseases (131)
- Nutritional and Metabolic Diseases (131)