NCT06539169
- Conditions
- Alpha-Thalassemia, Alzheimer Disease, Amyloidosis, +104 more
- Locations
-
- xCures Los Altos, California, United States
Clinical trial condition
Gaucher Disease
Explore clinical trials studying Gaucher Disease. Study availability and eligibility vary by location and protocol.
133 public trials
23 recruiting studies
Gaucher Disease trial results
NCT03240653
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- Birmingham Childrens Hospital Birmingham, United Kingdom
- New Queen Elizabeth Hospital Birmingham, United Kingdom
- Cambridge University Hospital Cambridge, United Kingdom
- Great Ormond Street Hospital London, United Kingdom
NCT06272149
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- Xinhua Hospital Affiliated to Shanghai Jiao Tong University School of Medicine Shanghai, Shanghai Municipality, China
Not yet recruiting
4SCAR-T Therapy Targeting GD2, PSMA and CD276 for Treating Neuroblastoma
NCT04637503
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +24 more
- Locations
-
- Shenzhen Geno-Immune Medical Institute Shenzhen, Guangzhou, China
Not yet recruiting
Study to Evaluate the Efficacy and Safety of Nizubaglustat (AZ-3102) in Patients With Gaucher Disease Type 3 (GD3)
NCT07715084
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- SMS Medical College Jaipur Jaipur, India
- Maula a Azad medical college Delhi New Delhi, India
- Sir Ganga Ram Hospital New Delhi, India
- University of Child Health Sciences and the Children's Hospital Lahore, Pakistan
Not yet recruiting
A Phase I/II Clinical Study to Evaluate the Safety and Efficacy of VGN-R08b in Patients With Type III Gaucher's Disease
NCT07603050
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
Not specified
Not yet recruiting
A Survey to Assess Participants', Caregivers', and Nurses' Use and Understanding of Educational Material on Velaglucerase Alfa (VPRIV) Home Infusion
NCT05669729
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
-
Not specified
Not yet recruiting
Efficacy and Safety of Eliglustat in Chinese Pediatric Patients With Gaucher Disease Type 1 and Type 3
NCT06523517
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
-
- Peking union medical college hospital Beijing, China
Not yet recruiting
Screening for Gaucher Disease and Acid Sphingomyelinase Deficiency
NCT06258577
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
-
- China Medical University Hospita Taichung, Taiwan
Enrolling by invitation
Genetic Studies of Lysosomal Storage Disorders
NCT00001215
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +21 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Related conditions
- Brain Diseases (133)
- Brain Diseases, Metabolic (133)
- Brain Diseases, Metabolic, Inborn (133)
- Central Nervous System Diseases (133)
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities (133)
- Lysosomal Storage Diseases, Nervous System (133)
- Nervous System Diseases (133)
- Nutritional and Metabolic Diseases (133)