NCT02699190
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
-
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
Clinical trial condition
Gangliosidoses, GM2
Explore clinical trials studying Gangliosidoses, GM2. Study availability and eligibility vary by location and protocol.
19 public trials
5 recruiting studies
Gangliosidoses, GM2 trial results
NCT05109793
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- Mayo Clinic Rochester Rochester, Minnesota, United States
- Hospital Pequeno Principe Curitiba, Brazil
- Hospital de Clinicas de Porto Alegre Porto Alegre, Brazil
NCT03759665
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
- Locations
-
- University of California - Los Angeles Los Angeles, California, United States
- Mayo Clinic Rochester, Minnesota, United States
- NYU Langone School of Medicine New York, United States
- University of Giessen Giessen, Germany
NCT04084301
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +32 more
- Locations
-
- Lukas Lannemyr Gothenburg, Västra Götaland County, Sweden
NCT04470713
- Conditions
- AB Variant Gangliosidosis GM2, Brain Diseases, Brain Diseases, Metabolic, +24 more
- Locations
-
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Mayo Clinic - Rochester Rochester, Minnesota, United States
- Lysosomal and Rare Disorders Research and Treatment Center Fairfax, Virginia, United States
- UCL Cliniques Universitaires Saint-Luc Brussels, Belgium
NCT00418847
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
- Locations
-
- The Hospital for Sick Children Toronto, Ontario, Canada
Completed
Gene Therapy for Tay-Sachs Disease
NCT01869270
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Data Management and Coordinating Center (DMCC), Univ. of South Florida Tampa, Florida, United States
- University of Minnesota Minneapolis, Minnesota, United States
Completed
Pyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease)
NCT01102686
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +17 more
- Locations
-
- The Hospital for Sick Children Toronto, Ontario, Canada
NCT00672022
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
- Locations
-
- Children's National Medical Center Washington D.C., District of Columbia, United States