NCT01757184
- Conditions
- Cholesterol Ester Storage Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
- Locations
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- Tucson, Arizona, United States
- Palo Alto, California, United States
- San Francisco, California, United States
- Wilmington, Delaware, United States