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Clinical trial condition

Brain Diseases, Metabolic

Explore clinical trials studying Brain Diseases, Metabolic. Study availability and eligibility vary by location and protocol.

1,103 public trials 225 recruiting studies
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Brain Diseases, Metabolic trial results

Completed

Copper Concentration & Histopathologic Changes in Liver Biopsy in Participants With Wilson Disease Treated With ALXN1840

NCT04422431

Conditions
Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +16 more
Locations
  • Research Site Sacramento, California, United States
  • Research Site Ann Arbor, Michigan, United States
  • Research Site Dallas, Texas, United States
  • Research Site Toronto, Ontario, Canada
View Trial Details
Completed

A Study of REPLAGAL® in Treatment-naive Chinese Participants With Fabry Disease

NCT04974749

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Peking Union Medical College Hospital Beijing, China
  • Xiangya Hospital, Central South University Changsha, China
  • West China Hospital, Sichuan University Chengdu, China
  • The Children's Hospital of Zhejiang University School of Medicine Hangzhou, China
View Trial Details
Completed

Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care

NCT02320084

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • Swedish Orphan Biovitrum Investigational Site Innsbruck, Austria
  • Swedish Orphan Biovitrum Investigational Site Vienna, Austria
  • Swedish Orphan Biovitrum Investigational Site Antwerp, Belgium
  • Swedish Orphan Biovitrum Investigational Site Brussels, Belgium
View all 77 locations
View Trial Details
Completed

To Evaluate the Safety of Long-term Use of HPN-100 in the Management of Urea Cycle Disorders (UCDs)

NCT01257737

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
Locations
  • UCLA Pediatrics/Genetics Los Angeles, California, United States
  • Stanford University School of Medicine Palo Alto, California, United States
  • Denver Children's Hospital Aurora, Colorado, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
View all 16 locations
View Trial Details
Completed

Efficacy and Safety of Lucerastat Oral Monotherapy in Adult Subjects With Fabry Disease

NCT03425539

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Alabama at Birmingham - Nephrology Research Clinic Birmingham, Alabama, United States
  • University of California Irvine Irvine, California, United States
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • University of Florida College of Medicine - Division of Nephrology, Hypertension & Renal Transplantation Gainesville, Florida, United States
View all 49 locations
View Trial Details
Completed

Phase 1b Study to Assess Safety, Tolerability, and Pharmacokinetics of ARCT-810 in Stable Adult Subjects With Ornithine Transcarbamylase Deficiency

NCT04442347

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +12 more
Locations
  • University of Florida Gainesville, Florida, United States
  • M Health Fairview Masonic Children's Hospital Minneapolis, Minnesota, United States
  • The Mount Sinai Hospital New York, United States
  • Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
View Trial Details
Completed

Study of the Safety and Tolerability of HPN-100 Compared to Sodium Phenylbutyrate in Children With Urea Cycle Disorders

NCT00947544

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +13 more
Locations
  • UCLA Los Angeles, California, United States
  • The George Washington DC Children's National Medical Center Washington D.C., District of Columbia, United States
  • Mount Sinai School of Medicine New York, United States
  • University of Pittsburgh Pittsburgh, Pennsylvania, United States
View Trial Details

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