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Clinical trial condition

Brain Diseases, Metabolic

Explore clinical trials studying Brain Diseases, Metabolic. Study availability and eligibility vary by location and protocol.

1,102 public trials 225 recruiting studies
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Brain Diseases, Metabolic trial results

Active, Not Recruiting

Arrhythmia Burden, Risk of Sudden Cardiac Death and Stroke in Patients With Fabry Disease

NCT03305250

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Sydney Sydney, Australia
  • University Hospitals Birmingham NHS Foundation Trust Birmingham, West Midlands, United Kingdom
  • Cambridge University Hospitals NHS Foundation Trust Cambridge, United Kingdom
  • Cardiff and Vale University Health Board Cardiff, United Kingdom
View Trial Details
Active, Not Recruiting

Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency:

NCT02616484

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
Locations
  • Children's Hospital of Orange County Orange, California, United States
  • Stanford University Stanford, California, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • University of Florida Gainesville, Florida, United States
View Trial Details
Active, Not Recruiting

Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product

NCT02698579

Conditions
Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +24 more
Locations
  • Mattel Children's Hospital-UCLA Los Angeles, California, United States
  • Lucile Packard Children's Hospital - Stanford Palo Alto, California, United States
  • Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
  • University of Minnesota Minneapolis, Minnesota, United States
View all 13 locations
View Trial Details
Active, Not Recruiting

AAV Gene Therapy Study for Subjects with PKU

NCT04480567

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • University of South Florida Tampa, Florida, United States
  • Morristown Medical Center Morristown, New Jersey, United States
  • University Hospital Birmingham NHS Foundation Trust Birmingham, United Kingdom
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Active, Not Recruiting

A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)

NCT04093349

Conditions
Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +17 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • University of California Irvine Health Orange, California, United States
  • Emory University School of Medicine Atlanta, Georgia, United States
  • University of Kansas Medical Center Research Institute Kansas City, Kansas, United States
View all 29 locations
View Trial Details
Active, Not Recruiting

Pegtibatinase As an Enzyme Therapy for Patients with Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (COMPOSE)

NCT03406611

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +12 more
Locations
  • Travere Investigational Site - Virtual Site Culver City, California, United States
  • Travere Investigational Site Aurora, Colorado, United States
  • Travere Investigational Site Miami, Florida, United States
  • Travere Investigational Site Indianapolis, Indiana, United States
View Trial Details

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