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Clinical trial condition

Brain Diseases, Metabolic

Explore clinical trials studying Brain Diseases, Metabolic. Study availability and eligibility vary by location and protocol.

1,103 public trials 225 recruiting studies
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Brain Diseases, Metabolic trial results

Completed

A Study of Intrathecal SHP611 in Children With Metachromatic Leukodystrophy

NCT03771898

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Los Angeles Biomedical Research Institute at Harbor-UCLA Torrance, California, United States
  • Childrens Hospital Colorado Aurora, Colorado, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View all 30 locations
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Completed

A Phase 2b Study of Zagociguat in Patients With MELAS

NCT06402123

Conditions
Acid-Base Imbalance, Acidosis, Acidosis, Lactic, +23 more
Locations
  • UC San Diego - Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Children's Hospital of Colorado Aurora, Colorado, United States
  • Rare Disease Research Atlanta, Georgia, United States
  • Massachusetts General Hospital Boston, Massachusetts, United States
View all 20 locations
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Completed

Safety and Efficacy of Eliglustat With or Without Imiglucerase in Pediatric Patients With Gaucher Disease (GD) Type 1 and Type 3

NCT03485677

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
Locations
  • Investigational Site Number : 0320001 Buenos Aires, Argentina
  • Investigational Site Number : 1240002 Calgary, Alberta, Canada
  • Investigational Site Number : 1240003 Vancouver, British Columbia, Canada
  • Investigational Site Number : 1240001 Toronto, Ontario, Canada
View all 21 locations
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Completed

A Gene Therapy Study in Patients With Gaucher Disease Type 1

NCT05324943

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • Kaiser Permanente Los Angeles, California, United States
  • Lysosomal Rare Disorders Research and Treatment Center Fairfax, Virginia, United States
  • Hospital de Clinicas de Porto Alegre (HCPA) Porto Alegre, Brazil
  • SphinCS Höchheim, Germany
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