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Clinical trial condition

Brain Diseases, Metabolic

Explore clinical trials studying Brain Diseases, Metabolic. Study availability and eligibility vary by location and protocol.

1,103 public trials 225 recruiting studies
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Brain Diseases, Metabolic trial results

Recruiting

Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)

NCT06150716

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +12 more
Locations
  • Ionis Investigative Site Atlanta, Georgia, United States
  • Ionis Investigative Site Philadelphia, Pennsylvania, United States
  • Ionis Investigative Site Salt Lake City, Utah, United States
  • Ionis Investigative Site Le Kremlin-Bicêtre, France
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Recruiting

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

NCT06332807

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +9 more
Locations
  • Children's Hospital of Orange County Hospital Orange, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Atlantic Health System Morristown, New Jersey, United States
  • University of Pittsburgh Medical Center Pittsburgh, Pennsylvania, United States
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Recruiting

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

NCT06663358

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • Emory University School of Medicine Atlanta, Georgia, United States
  • Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of Iowa Hospitals and Clinics Iowa City, Iowa, United States
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Recruiting

A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)

NCT06192576

Conditions
Acid Sphingomyelinase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +19 more
Locations
  • Ann and Robert H Lurie Children's Hospital of Chicago- Site Number: 001002 Chicago, Illinois, United States
  • Children's Hospital Medical Center- Site Number: 001003 Cincinnati, Ohio, United States
  • Nationwide Children's Hospital - PIN- Site Number : 1001-1 Columbus, Ohio, United States
  • Pulse InfoFrame US Inc.- Site Number: 001001 Philadelphia, Pennsylvania, United States
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