Completed
A Study of Potential Treatment-Responsive Biomarkers and Clinical Outcomes in Hunter Syndrome
NCT04007536
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +22 more
- Locations
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- UCSF Benioff Children's Hospital Oakland, California, United States
- UNC Children's Research Institute Chapel Hill, North Carolina, United States
- UPMC | Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
- Erasmus Medical Center Rotterdam, South Holland, Netherlands