Completed
Safety Dose Finding Study of ADVM-043 Gene Therapy to Treat Alpha-1 Antitrypsin (A1AT) Deficiency
NCT02168686
- Conditions
- Alpha 1-Antitrypsin Deficiency, Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- University of Florida Gainesville, Florida, United States
- Medical University of South Carolina Charleston, South Carolina, United States