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Clinical trial condition

Spinal muscular atrophy with respiratory distress 1

Explore clinical trials studying Spinal muscular atrophy with respiratory distress 1. Study availability and eligibility vary by location and protocol.

4 public trials 1 recruiting study

Spinal muscular atrophy with respiratory distress 1 trial results

NCT04292574

Conditions
Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • John Walton Muscular Dystrophy Research Centre Newcastle upon Tyne, United Kingdom
Conditions
Amyotrophic Lateral Sclerosis, Central Nervous System Diseases, Charcot-Marie-Tooth Disease, +28 more
Locations
  • Nemours Children's Hospital Delaware Wilmington, Delaware, United States
  • Nemours Children's Specialty Care Jacksonville, Florida, United States
  • Nemours Children's Hospital Orlando Orlando, Florida, United States
Conditions
Distal Hereditary Motor Neuronopathy Type I, Distal Hereditary Motor Neuronopathy Type VI, Distal Hereditary Motor Neuropathy, Type II, +4 more
Locations
  • Queen Square centre for Neuromuscular Diseases London, Greater London, United Kingdom