NCT05430113
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
- Locations
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- University of Pittsburgh Pittsburgh, Pennsylvania, United States
Clinical trial condition
Explore clinical trials studying Spinal Muscular Atrophy Type 4. Study availability and eligibility vary by location and protocol.
NCT05430113