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Clinical trial condition

Spinal Muscular Atrophies of Childhood

Explore clinical trials studying Spinal Muscular Atrophies of Childhood. Study availability and eligibility vary by location and protocol.

48 public trials 8 recruiting studies
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Spinal Muscular Atrophies of Childhood trial results

Not Yet Recruiting

A Phase I/II Clinical Study to Evaluate SKG0201 Injection in Subjects With Spinal Muscular Atrophy Type I

NCT07554924

Conditions
Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
Locations
  • Peking University First Hospital Beijing, Beijing Municipality, China
  • Children's Hospital of Fudan University Shanghai, Shanghai Municipality, China
  • Children's Hospital, Zhejiang University School of Medicine Hangzhou, Zhejiang, China
View Trial Details
Completed

Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies

NCT03837184

Conditions
Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
Locations
  • Tokyo Women's Medical University Tokyo, Japan
  • Pusan National University Yangsan Hospital Yangsan, Gyeongsangnam-do, South Korea
  • Seoul National University Hospital Seoul, South Korea
  • National Taiwan University Hospital Taipei, Taiwan
View Trial Details
Completed

Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam

NCT05156320

Conditions
Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
Locations
  • Children's of Alabama Birmingham, Alabama, United States
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • Stanford University Medical Center Palo Alto, California, United States
View all 50 locations
View Trial Details
Completed

Efficacy and Safety of Intrathecal OAV101 (AVXS-101) in Pediatric Patients With Type 2 Spinal Muscular Atrophy (SMA)

NCT05089656

Conditions
Atrophy, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +18 more
Locations
  • Connecticut Children's Medical Center Farmington, Connecticut, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Clinic for Special Children Strasburg, Pennsylvania, United States
  • St Jude Children's Research Hospital Memphis, Tennessee, United States
View all 42 locations
View Trial Details
Completed

An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy

NCT03921528

Conditions
Atrophy, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +19 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Stanford University Palo Alto, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • The Johns Hopkins University Baltimore, Maryland, United States
View all 16 locations
View Trial Details

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