NCT02292537
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- UCLA Clinical and Translational Research Center Los Angeles, California, United States
- Lucile Packard Children's Hospital at Stanford Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Nemours Children's Hospital Orlando, Florida, United States