Active, not recruiting
Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients
NCT05901987
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
-
- Peking University， First Hospital, Department of Pediatrics Beijing, China
- Bayi Children's Hospital, Seventh Medical Center, PLA general hospital Beijing, China
- West China Second University Hospital, Sichuan University Chengdu, China
- Children's Hospital of Chongqing Medical University Chongqing, China