Skip to main content
OpenTrials

Clinical trial condition

SMA

Explore clinical trials studying SMA. Study availability and eligibility vary by location and protocol.

15 public trials 4 recruiting studies

SMA trial results

Conditions
Anti-myostatin, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +17 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Children's Hospital of Orange County (CHOC) Orange, California, United States
  • Stanford Neuroscience Health Center (SNHC) Palo Alto, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
View all 25 locations
Conditions
BMD, Congenital Muscular Dystrophy, DMD, +2 more
Locations
  • Cantonal Hospital Aarau Aarau, Canton of Aargau, Switzerland
  • Pediatric Institute of Southern Switzerland, Ospedale San Giovanni Bellinzona, Canton Ticino, Switzerland
  • Neuro Centre of Italian Switzerland, Ospedale Regionale di Lugano Lugano, Canton Ticino, Switzerland
  • University Hospital Lausanne CHUV, Children's Hospital Lausanne, Vaude, Switzerland
View all 19 locations

NCT04292574

Conditions
Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • John Walton Muscular Dystrophy Research Centre Newcastle upon Tyne, United Kingdom
Conditions
Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
Locations
  • Children's of Alabama Birmingham, Alabama, United States
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • Stanford University Medical Center Palo Alto, California, United States
View all 50 locations
Conditions
Atrophy, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +19 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Stanford University Palo Alto, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • The Johns Hopkins University Baltimore, Maryland, United States
View all 16 locations