Active, Not Recruiting
A Study Evaluating the Safety and Efficacy of EDIT-301 in Participants With Severe Sickle Cell Disease (RUBY)
NCT04853576
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Smilow Cancer Hospital New Haven, Connecticut, United States
- Johns Hopkins All Children's Hospital St. Petersburg, Florida, United States