NCT01509768
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Children's Hospital and Research Center Oakland, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Johannes Gutenberg University Medical Center Mainz, Germany
- Great Ormond Street Hospital for Children London, United Kingdom