Active, not recruiting
Phase 1 Study of GC1130A in Patients With Sanfilippo Syndrome Type A (MPS IIIA)
NCT06567769
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
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- UCSF Benioff Children's Hospital Oakland, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Ajou University Medical Center Suwon, Gyeongi-do, South Korea
- Samsung Medical Center Seoul, South Korea