Completed
Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy
NCT02053064
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +13 more
- Locations
-
- Hôpitaux Universitaires Paris Sud (Bicêtre) Le Kremlin-Bicêtre, France