Recruiting
Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD)
NCT01668186
- Conditions
- ACBD5 (AcylCoA Binding Domain 5) Deficiency, ATP Binding Cassette Subfamily D Member 3 Gene Mutation, Abnormalities, Multiple, +48 more
- Locations
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- Research Institute of the McGill University Health Center Montreal, Quebec, Canada