Active, Not Recruiting
A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)
NCT03913143
- Conditions
- Blindness, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +26 more
- Locations
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- University of Iowa Iowa City, Iowa, United States
- Universitair Ziekenhuis Gent (UZ) Ghent, Belgium
- INRET Clínica/ Santa Casa de Misericórdia de Belo Horizonte Belo Horizonte, Minas Gerais, Brazil
- Federal University of São Paulo - Hospital São Paulo (UNIFESP-HSP) São Paulo, Brazil