NCT05619900
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +36 more
- Locations
-
- University of California San Francisco San Francisco, California, United States
Clinical trial condition
Pompe Disease Infantile-Onset
Explore clinical trials studying Pompe Disease Infantile-Onset. Study availability and eligibility vary by location and protocol.
5 public trials
2 recruiting studies
Pompe Disease Infantile-Onset trial results
NCT04532047
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +39 more
- Locations
-
- University of California San Francisco, California, United States
Completed
MSOT in Pompe Disease
NCT05083806
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- University Hospital Erlangen Erlangen, Bavaria, Germany
NCT00763932
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- Children's Hospital of Oakland Oakland, California, United States
- Children's Hospital of Orange Country Orange, California, United States
- University of Nebraska Medical Center Omaha, Nebraska, United States
- Institute for Genetic Medicine, Saint Peter's University Hospital New Brunswick, New Jersey, United States
Active, Not Recruiting
Evaluation of the Safety and Efficacy of Infantile-onset Pompe Disease Gene Therapy Drug
NCT05793307
- Conditions
- Pompe Disease Infantile-Onset
- Locations
-
- Peking Union Medical College Beijing, China
- 301 Chinese PLA General Hospital Beijing, China
- Central South University, Xiangya Hospital Changsha, China
- Zhejiang University, School of Medicine, The Children's Hospital Hangzhou, China
Related conditions
- Brain Diseases (4)
- Brain Diseases, Metabolic (4)
- Brain Diseases, Metabolic, Inborn (4)
- Carbohydrate Metabolism, Inborn Errors (4)
- Central Nervous System Diseases (4)
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4)
- Genetic Diseases, Inborn (4)
- Lysosomal Storage Diseases, Nervous System (4)