Active, Not Recruiting
A Phase 1/Phase 2 Open-label Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Intravenous Administration of SAR444836 in Adult Participants With Phenylketonuria
NCT05972629
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
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- University of California San Francisco- Site Number : 8400007 San Francisco, California, United States
- Children's Hospital IMD Clinic- Site Number : 8400015 Aurora, Colorado, United States
- University of Florida-Genetics- Site Number : 8400010 Gainesville, Florida, United States
- UHCMC- Site Number : 8400014 Cleveland, Ohio, United States