Active, Not Recruiting
A Study to Evaluate the Efficacy and Safety of Mitapivat in Pediatric Participants With Pyruvate Kinase Deficiency (PKD) Who Are Not Regularly Transfused, Followed by a 5-Year Extension Period
NCT05175105
- Conditions
- Anemia, Hematologic Diseases, Hemic and Lymphatic Diseases, +5 more
- Locations
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- Stanford Medicine Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Children's Healthcare of Atlanta - Emory Atlanta, Georgia, United States
- UChicago Medicine Chicago, Illinois, United States