Enrolling by Invitation
Long-Term Follow Up Study of Subjects Previously Administered HMI 102
NCT04348708
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +11 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
- Icahn School of Medicine at Mount Sinai New York, United States