Completed
Miglustat in Niemann-Pick Type C Disease
NCT00517153
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
Not specified
Clinical trial condition
Niemann-Pick Disease, Type C
Explore clinical trials studying Niemann-Pick Disease, Type C. Study availability and eligibility vary by location and protocol.
22 public trials
6 recruiting studies
Niemann-Pick Disease, Type C trial results
NCT03759639
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Mayo Clinic Rochester, Minnesota, United States
- University of Giessen Giessen, Germany
- Ludwig Maximilian University of Munich München, Germany
- Comenius University in Bratislva Bratislava, Slovakia
NCT02534844
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +34 more
- Locations
-
- University of Alabama at Birmingham Birmingham, Alabama, United States
- Children's Hospital of Orange County Orange, California, United States
- University of California San Francisco San Francisco, California, United States
- University of Colorado Denver Aurora, Colorado, United States
NCT02912793
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Soroka Mc Beersheba, Rager Blvd, Israel
- HaeMek MC Afula, Israel
- Karolinska Trial Alliance Solna, Huddinge, Sweden
- Salford Royal Hospital Salford, Greater Manchester, United Kingdom
NCT01747135
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
NCT02939547
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland Oakland, California, United States
- Atlantic Health System/Morristown Medical Center Morristown, New Jersey, United States
NCT02124083
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +21 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
Completed
A Prospective Non-therapeutic Study in Patients Diagnosed With Niemann-Pick Disease Type C
NCT02435030
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- University Hospital Copenhagen (Rigshospitalet) Copenhagen, Denmark
- CHU de Montpellier Montpellier, France
- Hôpital Trousseau Paris, France
- Villa Metabolica Mainz Mainz, Germany
NCT01899950
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Mayo Clinic Rochester, Minnesota, United States
Completed
Biomarker Validation for Niemann-Pick Disease, Type C: Safety and Efficacy of N-Acetyl Cysteine
NCT00975689
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +22 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States