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Clinical trial condition

Niemann-Pick Disease, Type A

Explore clinical trials studying Niemann-Pick Disease, Type A. Study availability and eligibility vary by location and protocol.

9 public trials 1 recruiting study

Niemann-Pick Disease, Type A trial results

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • UCSF Medical Center Site Number : 840005 San Francisco, California, United States
  • Emory University Site Number : 840003 Decatur, Georgia, United States
  • Montefiore Medical Center Site Number : 840006 The Bronx, New York, United States
  • Investigational Site Number : 032001 Córdoba, Argentina
View all 24 locations
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • Investigational Site Number 840001 New York, United States
  • Investigational Site Number 056001 Leuven, Belgium
  • Investigational Site Number 076001 Porto Alegre, Brazil
  • Investigational Site Number 250002 Bron, France
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • Investigational Site Number :8400002 Atlanta, Georgia, United States
  • Investigational Site Number :8400003 The Bronx, New York, United States
  • Investigational Site Number :8400001 Valhalla, New York, United States
  • Investigational Site Number :0320002 CABA, Argentina
View all 28 locations
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • Investigational Site Number 840001 New York, United States
  • Investigational Site Number 076001 Porto Alegre, Brazil
  • Investigational Site Number 250002 Bron, France
  • Investigational Site Number 276001 Mainz, Germany

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States