Enrolling by Invitation
A Study of Long-term Safety and Efficacy of VX-670 in Participants With Myotonic Dystrophy Type I
NCT06926621
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +15 more
- Locations
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- Wesley Research Institute Auchenflower, Australia
- Neuroscience Clinical Trials Unit, Alfred Brain Melbourne, Australia
- Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg - Pulmonology Leuven, Belgium
- Altasciences Montreal Montreal, Canada