Completed
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
NCT05479981
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
- Locations
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- University of California Los Angeles Los Angeles, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States