Active, Not Recruiting
Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi
NCT04042025
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +12 more
- Locations
-
- Stanford University Medical Center Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Ann Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- John Hopkins Hospital - David M. Rubenstein Child Health Building Baltimore, Maryland, United States