NCT03409003
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
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- Children's National Medical Center Washington D.C., District of Columbia, United States
- Children's Hospital Boston (UCDC New England Center) Boston, Massachusetts, United States
- Icahn School of Medicine at Mount Sinai New York, United States