Recruiting
Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy
NCT06503367
- Conditions
- LAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A), Muscular dystrophy congenital, merosin negative
- Locations
-
- University of California, Los Angeles Los Angeles, California, United States
- Stanford University Stanford, California, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- University of Iowa Stead Family Children's Hospital Iowa City, Iowa, United States