Active, Not Recruiting
Open-label Extension of the HOPE-2 Trial
NCT04428476
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- University of California, Davis Sacramento, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Washington University St Louis, Missouri, United States
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States