- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +14 more
- Locations
-
- Manchester Academic Health Science Centre Manchester, United Kingdom
Clinical trial condition
Mucopolysaccharidosis VII
Explore clinical trials studying Mucopolysaccharidosis VII. Study availability and eligibility vary by location and protocol.
14 public trials
4 recruiting studies
Mucopolysaccharidosis VII trial results
NCT01043640
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +52 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Active, Not Recruiting
Early Check: Expanded Screening in Newborns
NCT03655223
- Conditions
- 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
- Locations
-
- RTI International Research Triangle Park, North Carolina, United States
Active, Not Recruiting
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
NCT02171104
- Conditions
- Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Related conditions
- Carbohydrate Metabolism, Inborn Errors (14)
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities (14)
- Connective Tissue Diseases (14)
- Genetic Diseases, Inborn (14)
- Mucinoses (14)
- Nutritional and Metabolic Diseases (14)
- Skin and Connective Tissue Diseases (14)
- Metabolism, Inborn Errors (13)