Active, not recruiting
Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A)
NCT06181136
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
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- UCSF Benioff Children's Hospital Oakland Oakland, California, United States
- University of Iowa Stead Family Children's Hospital Iowa City, Iowa, United States
- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
- Baylor College of Medicine and Texas Children's Hospital Houston, Texas, United States