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OpenTrials

Clinical trial condition

Mucopolysaccharidosis IV

Explore clinical trials studying Mucopolysaccharidosis IV. Study availability and eligibility vary by location and protocol.

77 public trials 19 recruiting studies

Mucopolysaccharidosis IV trial results

NCT06036693

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +33 more
Locations
  • Centre Hospitalier Universitaire d'Angers Angers, France
  • Hôpital des Enfants - Groupe Hospitalier Pellegrin Bordeaux, France
  • Hôpital Morvan Brest, France
  • Hôpital d'Estaing Clermont-Ferrand, France
View all 23 locations
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +13 more
Locations
  • Children'S Hospital of Orange County Orange, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Saint Louis University St Louis, Missouri, United States
Conditions
Acid Sphingomyelinase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +65 more
Locations
  • Maimonides Medical Center Brooklyn, New York, United States
  • NYU Langone Hospital - Brooklyn Brooklyn, New York, United States
  • North Shore University Hospital Manhasset, New York, United States
  • NYU Langone Health - Tisch Hospital New York, United States