Not Yet Recruiting
A Phase I/II Trial of JR-446 in Mucopolysaccharidosis Type IIIB (MPS IIIB)
NCT07640984
- Conditions
- Mucopolysaccharidosis IIIB
- Locations
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- Children's Hospital Oakland Research Institution, Attn: 2900 Wing Oakland, California, United States
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
- Lysosomal and Rare Disorders Research and Treatment Center (LDRTC) Fairfax, Virginia, United States
- University Medical Center Hamburg-Eppendorf Hamburg, Germany