Enrolling by Invitation
Follow-up Study of AAV-Mediated Gene Transfer (UX111; Previously Known as ABO-102) for MPS Type IIIA
NCT04360265
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +13 more
- Locations
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- Nationwide Children's Hospital Columbus, Ohio, United States
- Women's and Children's Hospital North Adelaide, South Australia, Australia
- Vall d'Hebron Barcelona Campus Barcelona, Spain
- Hospital Clínico Universitario de Santiago Santiago de Compostela, Spain