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Clinical trial condition

Mucopolysaccharidosis III

Explore clinical trials studying Mucopolysaccharidosis III. Study availability and eligibility vary by location and protocol.

4 public trials 3 recruiting studies

Mucopolysaccharidosis III trial results

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
Locations
  • Nationwide Children's Hospital Columbus, Ohio, United States
  • Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
  • Women's and Children's Hospital North Adelaide, South Australia, Australia
  • Vall d'Hebron Barcelona Hospital Campus Barcelona, Spain
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • The Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center Torrance, California, United States

NCT06036693

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +33 more
Locations
  • Centre Hospitalier Universitaire d'Angers Angers, France
  • Hôpital des Enfants - Groupe Hospitalier Pellegrin Bordeaux, France
  • Hôpital Morvan Brest, France
  • Hôpital d'Estaing Clermont-Ferrand, France
View all 23 locations
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • The Lundquist Institute at Harbor-UCLA Medical Center Torrance, California, United States