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Clinical trial condition

Mucopolysaccharidosis III

Explore clinical trials studying Mucopolysaccharidosis III. Study availability and eligibility vary by location and protocol.

42 public trials 7 recruiting studies
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Mucopolysaccharidosis III trial results

Completed

Open-label Study of Anakinra in MPS III

NCT04018755

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • The Lundquist Institute at Harbor-UCLA Medical Center Torrance, California, United States
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Completed

A Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients

NCT03811028

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Children´s Hospital and research center Oakland, California, United States
  • University of North Carolina hospitals Chapel Hill, North Carolina, United States
  • Gazi University Hospital Ankara, Turkey (Türkiye)
View Trial Details
Completed

A Study to Assess the Safety and Tolerability of SOBI003 in Pediatric MPS IIIA Patients

NCT03423186

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Childrens's Hospital and Research Center Oakland, California, United States
  • University of North Carolina Hospitals Chapel Hill, North Carolina, United States
  • University Medical Center Hamburg-Eppendorf Hamburg, Germany
  • Gazi University Hospital Ankara, Turkey (Türkiye)
View Trial Details
Completed

Randomized, Controlled, Open-label, Multicenter, Safety and Efficacy Study of rhHNS Administration Via an IDDD in Pediatric Patients With Early Stage MPS IIIA Disease

NCT02060526

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +18 more
Locations
  • Los Angeles Biomedical Research Torrance, California, United States
  • University of Minnesota Department of Pediatrics Minneapolis, Minnesota, United States
  • University of North Carolina Chapel Hill, North Carolina, United States
  • Hospital Universitario Austral A Unidad de Investigacion Buenos Aires, Argentina
View Trial Details
Completed

Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)

NCT01509768

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Children's Hospital and Research Center Oakland, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Johannes Gutenberg University Medical Center Mainz, Germany
  • Great Ormond Street Hospital for Children London, United Kingdom
View Trial Details
Completed

A Treatment Study of Mucopolysaccharidosis Type IIIB

NCT02754076

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • Fundación Cardio Infantil - Instituto de Cardiología Bogotá, Colombia
  • University Medical Center Hamburg Eppendorf, Department of Pediatrics Hamburg, Germany
  • Hospital Clinico Universitario de Santiago Santiago de Compostela, Spain
View Trial Details
Completed

A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)

NCT02493998

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +13 more
Locations
  • Children's Hospital and Research Center Oakland Oakland, California, United States
  • Melbourne Children's Trials Centre Melbourne, Victoria, Australia
  • Fundacion Cardioinfantil-Instituto de Cardiologia Bogotá, Colombia
  • University Medical Center Hamburg Eppendorf, Department of Pediatrics Hamburg, Germany
View Trial Details

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