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Clinical trial condition

Mucopolysaccharidoses

Explore clinical trials studying Mucopolysaccharidoses. Study availability and eligibility vary by location and protocol.

39 public trials 5 recruiting studies
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Mucopolysaccharidoses trial results

Completed

Observational Study to Evaluate Neurodevelopmental Status in Pediatric Patients With Hunter Syndrome (MPS II)

NCT01822184

Conditions
Carbohydrate Metabolism, Inborn Errors, Cognition Disorders, Cognitive Dysfunction, +25 more
Locations
  • Childrens Hospital & Research Center Oakland Oakland, California, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of North Carolina Division of Genetics and Metabolism Chapel Hill, North Carolina, United States
  • Hospital Universitario Austral Pilar, Buenos Aires, Argentina
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Completed

A Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7)

NCT02432144

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Baylor College of Medicine Houston, Texas, United States
View Trial Details
Completed

A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)

NCT02230566

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Miami Children's Hospital Miami, Florida, United States
  • University of Minnesota Minneapolis, Minnesota, United States
View Trial Details
Completed

Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) Patients Less Than 5 Years of Age

NCT02418455

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
Locations
  • Children's National Health System Washington D.C., District of Columbia, United States
  • New York University Langone Medical Center New York, United States
  • University of Utah Hospital Salt Lake City, Utah, United States
  • Centro Hospitalar do Porto Porto, Portugal
View Trial Details

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