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Clinical trial condition

Mucopolysaccharidoses

Explore clinical trials studying Mucopolysaccharidoses. Study availability and eligibility vary by location and protocol.

193 public trials 26 recruiting studies
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Mucopolysaccharidoses trial results

Completed

Study of Long Term Safety and Clinical Outcomes of Idursulfase IT and Elaprase Treatment in Pediatric Participants Who Have Completed Study HGT-HIT-094

NCT02412787

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • Children's Hospital and Research Center at Oakland Oakland, California, United States
  • Ann & Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of North Carolina Chapel Hill, North Carolina, United States
  • Women's and Children's Hospital Adelaide, Australia
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Completed

A Study of JR-171 in Patients With Mucopolysaccharidosis I

NCT04227600

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Hospital de Clínicas de Porto Alegre Porto Alegre, Brazil
  • Instituto de Genética e Erros Inatos do Metabolismo - IGEIM São Paulo, Brazil
  • Fukuoka Children's Hospital Fukuoka, Japan
View Trial Details
Completed

A Study of Elaprase in Children and Adults With Hunter Syndrome (Mucopolysaccharidosis II) in India

NCT05058391

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • SAT Hospital - Govt Medical College Thiruvananthapuram, Kerala, India
  • JK Lone Hospital Jaipur, Rajasthan, India
  • Institute of Child Health Kolkata, India
  • All India Institute of Medical Sciences (AIIMS) New Delhi, India
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Completed

Gene Therapy in Patients With Mucopolysaccharidosis Disease

NCT03173521

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Department of Translational Medicine (DISMET) of "Federico II" University, Naples Naples, Italy
  • Children's Hospital Hacettepe University Ankara, Turkey (Türkiye)
View Trial Details
Completed

Hunter Outcome Survey (HOS)

NCT03292887

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • Shire Lexington, Massachusetts, United States
View Trial Details

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