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Clinical trial condition

Mucopolysaccharidoses

Explore clinical trials studying Mucopolysaccharidoses. Study availability and eligibility vary by location and protocol.

193 public trials 26 recruiting studies
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Mucopolysaccharidoses trial results

Completed

A Study in MPS VI to Assess Safety and Efficacy of Odiparcil

NCT03370653

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • Hôpital Femme-Mère-Enfant Bron, France
  • Villa Metabolica Mainz, Germany
  • Centro Hospitalar S. João Porto, Portugal
  • Royal Free Hospital London, United Kingdom
View Trial Details
Completed

Gait Analysis in MPS IVA

NCT01920828

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more
Locations
  • Oregon Health and Science University Portland, Oregon, United States
View Trial Details
Completed

BMN 110 Phase 3B in Australian Patients

NCT01966029

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Children's Hospital at Westmead Westmead, New South Wales, Australia
  • Lady Cilento Children's Hospital (previous: Royal Children's Hospital) Brisbane, Queensland, Australia
  • Murdoch Childrens Research Institute and Royal Children's Hospital Melbourne, Victoria, Australia
  • Princess Margaret Hospital for Children Perth, Western Australia, Australia
View Trial Details
Completed

Stem Cell Transplant w/Laronidase for Hurler

NCT00176891

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
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Completed

Efficacy and Safety Evaluation of Recombinant Human Growth Hormone (r-hGH), Saizen®, on a Population of Children With Hypochondroplasia, Treated at Least 3 Years or Until Near Final Height, When Applicable, in Comparison With a Historic Cohort of Non-treated Children

NCT01111019

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Endocrinologie Pédiatrique - centre des maladies rares de la croissance -Hôpital Necker Enfants Malades Paris, France
View Trial Details
Completed

Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome

NCT02262338

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +22 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Emory University Decatur, Georgia, United States
  • ZKJM MC University of Mainz Mainz, Germany
View Trial Details

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