Enrolling by Invitation
Safety, Tolerability and Efficacy of ICV AX 250 Treatment in MPS IIIB -OLE
NCT05492799
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
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- UCSF Benioff Children's Hospital Oakland Oakland, California, United States
- UPMC Children's Hospital Pittburgh Pittsburgh, Pennsylvania, United States
- Fundación Cardio Infantil - Instituto de Cardiología Bogotá, Colombia
- University Medical Center Hamburg-Eppendorf Hamburg, Germany