NCT04532047
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +39 more
- Locations
-
- University of California San Francisco, California, United States
Clinical trial condition
MPS II
Explore clinical trials studying MPS II. Study availability and eligibility vary by location and protocol.
5 public trials
2 recruiting studies
MPS II trial results
NCT03333200
- Conditions
- ALD, Alpha-Mannosidosis, Batten Disease, +78 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
Completed
An Extension Study to Assess the Long-term Safety and Efficacy of Hunterase (Idursulfase Beta)
NCT07344376
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +27 more
- Locations
-
- Samsung Medical Center Seoul, South Korea
NCT00607386
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
- Locations
-
- Hospital de Clinicas de Porto Alegre, Servico de Genetica Medica Porto Alegre, Rio Grande do Sul, Brazil
- Instytut Pomnik Centrum Zdrowia Dziecka, Klinika Chorob Metaboliczynch, Endokrynologii i Diabetologii Warsaw, Poland
- National Taiwan University Hospital, Dept. of Pediatrics and Medical Genetics Taipei, Taiwan
Active, Not Recruiting
RGX-121-3102 Gene Therapy in Participants With MPS II (Hunter Syndrome)
NCT07236606
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
- Locations
-
- St. Peter's University Hospital New Brunswick, New Jersey, United States