Active, Not Recruiting
A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT
NCT06149403
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
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- University of Minnesota, Pediatrics Minneapolis, Minnesota, United States
- Ospedale San Raffaele Milan, Italy
- Princess Maxima Center Utrecht, Netherlands
- UMC Utrecht Utrecht, Netherlands