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Clinical trial condition

Mitochondrial Diseases

Explore clinical trials studying Mitochondrial Diseases. Study availability and eligibility vary by location and protocol.

226 public trials 38 recruiting studies
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Mitochondrial Diseases trial results

Completed

Open-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial Disease

NCT02023866

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +40 more
Locations
  • University of California at San Diego (UCSD) San Diego, California, United States
  • Stanford University Stanford, California, United States
  • Akron Children's Hospital Akron, Ohio, United States
  • Baylor College of Medicine Houston, Texas, United States
View Trial Details
Completed

Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia

NCT02415127

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +12 more
Locations
  • University of California, Los Angeles Neurology Clinic Los Angeles, California, United States
  • University of Florida - Clinical Research Center Gainesville, Florida, United States
  • University of Iowa Children's Hospital Iowa City, Iowa, United States
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
View Trial Details
Completed

Safety, Tolerability and Efficacy of ACTIMMUNE® Dose Escalation in Friedreich's Ataxia Study

NCT02593773

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +12 more
Locations
  • University of California, Los Angeles Neurology Clinic Los Angeles, California, United States
  • University of Florida - Clinical Research Center Gainesville, Florida, United States
  • University of Iowa Children's Hospital Iowa City, Iowa, United States
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
View Trial Details
Completed

Long-Term Safety Extension Study of ACTIMMUNE® (Interferon γ-1b) in Children and Young Adults With Friedreich's Ataxia

NCT02797080

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +12 more
Locations
  • University of California, Los Angeles Neurology Clinic Los Angeles, California, United States
  • University of Florida Clinical Research Center Gainesville, Florida, United States
  • University of Iowa Children's Hospital Iowa City, Iowa, United States
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
View Trial Details
Completed

Study to Evaluate QR-110 in Leber's Congenital Amaurosis (LCA) Due to the c.2991+1655A>G Mutation (p.Cys998X) in the CEP290 Gene

NCT03140969

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +14 more
Locations
  • University of Iowa Iowa City, Iowa, United States
  • Scheie Eye Institute, University of Pennsylvania Philadelphia, Pennsylvania, United States
  • Ghent University Hospital and Ghent University Ghent, Belgium
View Trial Details
Completed

Instrumented Data Exchange for Ataxia Study

NCT04268147

Conditions
Ataxia, Brain Diseases, Central Nervous System Diseases, +21 more
Locations
  • University of California-Los Angeles Los Angeles, California, United States
  • The University of Chicago Chicago, Illinois, United States
  • Johns Hopkins Medicine Baltimore, Maryland, United States
  • Mass General Hospital Boston, Massachusetts, United States
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