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Clinical trial condition

Metabolism, Inborn Errors

Explore clinical trials studying Metabolism, Inborn Errors. Study availability and eligibility vary by location and protocol.

2,496 public trials 457 recruiting studies
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Metabolism, Inborn Errors trial results

Completed

Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of SBC-102 (Sebelipase Alfa) in Adult Subjects With Lysosomal Acid Lipase Deficiency

NCT01488097

Conditions
Cholesterol Ester Storage Disease, Cholesterol Ester Storage Disease (CESD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
Locations
  • Eureka, California, United States
  • Sacramento, California, United States
  • San Francisco, California, United States
  • Minneapolis, Minnesota, United States
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Completed

ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)

NCT02319005

Conditions
Alzheimer Disease, Amyloid Neuropathies, Amyloid Neuropathies, Familial, +27 more
Locations
  • Clinical Trial Site Bakersfield, California, United States
  • Clinical Trial Site Beverly Hills, California, United States
  • Clinical Trial Site La Mesa, California, United States
  • Clinical Trial Site Los Angeles, California, United States
View all 61 locations
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Completed

A Study of the Efficacy of Canakinumab in Prevention of Acute Flares in Chronic Gout Patients Initiating Allopurinol Therapy (Core Study) and a Long-term Study of the Efficacy and Safety of Canakinumab in Patients With Gout (Extension Study)

NCT00819585

Conditions
Arthritis, Arthritis, Gouty, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
Locations
  • Talbert Medical Group Huntington Beach, California, United States
  • San Diego Arthritis & Osteoporosis Medical clinic San Diego, California, United States
  • Health Awareness Jupiter, Florida, United States
  • East-West Medical Research institute Honolulu, Hawaii, United States
View all 89 locations
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